Children's Health News, Features & Updates

Find out what could happen if a state struck down its requirement for middle school and high school students to get the meningitis vaccine.

A pediatrician answers the most common questions about meningitis in this Reddit AMA.

Alagille syndrome can affect your child’s health in a multitude of ways. Here’s what to know.

Learn how PFIC changes as children grow, what symptoms to watch for, and practical tips to help your child thrive at home and school.

When your child has Alagille syndrome, there may be many uncertainties about their future. Here’s what parents should know.

If you have a child who’s recently been diagnosed with PFIC, here’s where to go to find support and resources to help you manage their condition.

An artist with hypochondroplasia shares the story of her diagnosis, challenges, and experiences raising two daughters who also have this form of dwarfism.

A pediatric orthopedic surgeon explains the role he plays in treating symptoms and complications of hypochondroplasia.

Skeletal dysplasia experts explain how height-boosting medications for children with hypochondroplasia work and what the possible benefits and risks are.

Familial hyperchylomicronemia syndrome is a very rare condition with limited treatments available. Here’s a closer look at what life’s like with this condition.

If you have FCS, excess fats build up in your blood. An endocrinologist explains what you need to know about this rare genetic condition.

Living with familial hyperchylomicronemia is a challenge. A researcher and expert explains new treatments that may transform life with FCS.

Learn how plozasiran (Redemplo) works for familial chylomicronemia syndrome (FCS) and who it might help.

A top expert explains plozasiran (Redemplo) for familial chylomicronemia syndrome (FCS). Learn how this new treatment for FCS works, who it might help, and its impact on treatment.

New targeted drugs, gene therapy, and better immunoglobulin products are expanding treatment options for people with primary immunodeficiency diseases.

A Stanford immunologist answers key questions about living with primary immunodeficiency, including symptoms, vaccines, treatments, and mental health.

Caitlin BenVau was diagnosed with CVID at 13. Here's how she's built a career as a rocket engineer while managing primary immunodeficiency disease.

Learning how to advocate for your child with achondroplasia starts with these simple tips.

A leading expert shares his experience working with patients who live with this rare disease.

Art Estopinan was diagnosed with thymidine kinase 2 deficiency at 17 months old. Here's what he and his parents want you to know about this rare disease.

Recent treatment advances for thymidine kinase 2 deficiency (TK2d) are proving to be game changers. Here’s what’s new in the field.

Pediatric growth hormone deficiency may get easier to diagnose and treat in the future. Here’s what’s on the horizon.

Pediatric growth hormone deficiency (pGHD) can affect more than your child’s height. An expert explains what to know about this rare disease.

There’s a limited window where treatment is effective: for boys, it’s typically until around age 16, when the growth plates in their bones close.

Learn what everyday life is like for someone with achondroplasia dwarfism who competes in women's bodybuilding competitions.

Recent advances in achondroplasia management, including advances in medications and surgery, mean that more people can lead full, rewarding lives.

People with achondroplasia lead long, fulfilling lives. An expert talks about what to expect – including health complications – with this condition.

For Jordan Cantrell Smith, sometimes living with a condition like Duchenne muscular dystrophy means loving a child with it and using your voice when they can’t.

It’s normal to have a lot of questions if a loved one is diagnosed with this genetic disease. Learn who it affects, what are the symptoms, how it’s treated, and more.

People with Duchenne muscular dystrophy are living longer and better, thanks to advances in treatment.

A solid partnership with your child's care team is essential to treatment success for pLGG. Learn how to partner with them as you navigate your child's journey.

July 28, 2025 — Doptelet (avatrombopag) is a prescription medicine that helps the body make more platelets (cells that help stop bleeding). First approved in 2018 for adults, it is now also approved by the FDA for children aged 1 year or older with chronic immune thrombocytopenia (ITP) who haven’t gotten good responses from earlier treatments.

May 8, 2025 — With Mother’s Day approaching, we asked five top doctors for maternal health tips that showed just how smart their moms really were.

April 25, 2025 — As U.S. measles cases rise, a study suggests the disease could become endemic again – meaning bigger than an outbreak but not quite as big as a pandemic.

March 27, 2025 — The FDA has approved diazoxide choline (VYKAT XR) as a drug to treat hyperphagia, an uncontrollable urge to eat, in people with Prader-Willi syndrome, a rare life-threatening genetic disorder.

March 25, 2025 — Girls are twice as likely as boys to be diagnosed with depression, and researchers in London have now uncovered clues as to why.

March 20, 2025 — For the first time, scientists have found that babies are able to store memories in the brain region called the hippocampus. The ability appears to start around 1 year old.

Teaching kitchens are revolutionizing nutrition education, helping individuals of all ages adopt healthier eating habits and combat obesity.

March 10, 2025 — In early stages, measles can easily go undetected, putting you, your family, and your community at risk. Understand the signs and what to do if you notice them.

Get key insights from an expert on crinecerfont (Crenessity) for classic congenital adrenal hyperplasia. Learn about how this new drug for CAH works and who might benefit.

February 26, 2025 — The Texas Department of Health and Human Services says a school-age child who had been hospitalized in the West Texas town of Lubbock and was not vaccinated against measles has died in a measles outbreak.

February 21, 2025 — Measles cases surge in the United States, led by a significant outbreak in Texas, highlighting the need for increased MMR vaccination as recommended by the CDC.

February 3, 2025 — During the two quick years when a child is considered a preschooler, a diet high in ultraprocessed foods may put them at risk of developing overweight or obesity by the time they start kindergarten.

December 20, 2024 — The FDA has approved remestemcel-L, a new treatment for children age 2 months or older with steroid-refractory acute graft-versus-host disease (SR-aGVHD), a major complication of donor bone marrow transplantation.

December 20, 2024 — The FDA has approved olezarsen, a new drug that helps reduce high triglyceride levels in adults with a rare genetic condition called familial chylomicronemia syndrome (FCS).

December 17, 2024 — The FDA has approved crinecerfont, marketed under the brand name Crenessity, a first-in-class oral drug for treating classic congenital adrenal hyperplasia (CAH), a rare genetic condition present from birth.

November 18, 2024 — The FDA has granted fast-track approval for a groundbreaking gene therapy indicated for a rare genetic disorder called aromatic L-amino acid decarboxylase (AADC) deficiency.

October 16, 2024 — It may not sound surprising that treating obesity in adolescents and teens may have positive mental health impacts, but researchers this week reported reassuring findings about whether popular new injectable weight loss medicines carry mental health risks. Here's what to know.

September 26, 2024 — Within days of approving the first treatment for a rare genetic disorder, the FDA has approved another treatment for the same condition.